The very first priority I have when I have my legal judgment money is curing all malodorous rare diseases, including several that are neurodegenerative.  Since such small patient numbers are involved, I will be setting up a nonprofit pharmaceutical organization and giving away all FDA approved medications away for free as one-time curative treatments.  Clinical trials will take place in the US.

Maple Syrup Urine Disease
Isovaleric Acidemia 
Glutaric Acidemia Type I
Multiple Carboxylase Deficiency (Biotinidase Deficiency, Holocarboxylase Synnthetase Deficiency)
  3-Methylcrotonylglycinuria
Propionic Acidemia and Methylmalonic Acidemia
Hypermethioninemia (including Methionine Adenosyltransferase Deficiency)
Homocystinuria
Cystinuria
Glutaric Acidemia Type II (Multiple Acyl-CoA Dehydrogenase Deficiency)
Trimethylaminuria
Phenylketonuria
Tyrosinemia Type I
Hawkinsinuria
Dimethylglycinuria
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